Ornithine Carbamoyltransferase Deficiency Disease - 1 Studies Found
| Recruiting |
: Safety and Dose-Finding Study of DTX301 (scAAV8OTC) in Adults With Late-Onset OTC Deficiency : Ornithine Transcarbamylase (OTC) Deficiency : 2016-12-09 : Genetic: scAAV8OTC non-replicating, recombinant scAAV8 encoding human ornithine transcarbamylase (OTC) |