Medium-chain Acyl-coenzyme A Dehydrogenase Deficiency - 1 Studies Found
| Completed |
: Use of Ravicti™ in Patients With MCAD Deficiency With the 985A>G (K304E) Mutation : Medium-chain Acyl-CoA Dehydrogenase (MCAD) Deficiency : 2013-06-13 : Drug: Ravicti Open-label design comparing Ravicti at doses of 2, 4, and 6 grams/m2/day |