Leukodystrophy - 34 Studies Found
| Recruiting |
: Newborn Screening for Adrenoleukodystrophy : Adrenoleukodystrophy : 2016-10-31 : Procedure: newborns testing for ALD Routine newborn screening dried blood spots sample is used to test i |
| Withdrawn |
: MT2014-14 IT-MSC for Advanced Cerebral Adrenoleukodystrophy (cALD) : Cerebral Adrenoleukodystrophy : 2015-03-27 : Biological: Mesenchymal Stem Cells |
| Suspended |
: Effect of Glycerol Trierucate on Clinical Course of Adrenoleukodystrophy : Adrenoleukodystrophy : 1999-10-18 :
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| Available |
: Expanded Access for Lorenzo's Oil (GTO/GTE) in Adrenoleukodystrophy : X-linked Adrenoleukodystrophy : 2014-05-05 : Drug: Lorenzo's Oil Oral use of Lorenzo's oil to lower very long chain fatty acids |
| Available |
: Clinical Study and Gene Mutation Analysis of Adrenoleukodystrophy in Taiwanese Children : Adrenoleukodystrophy : 2006-01-16 : Procedure: blood sampling and medical records |
| Recruiting |
: A Phase 2/3 Study of the Efficacy and Safety of Hematopoietic Stem Cells Transduced With Lenti-D Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy (CALD) : Cerebral Adrenoleukodystrophy (CALD) : 2013-03-22 : Genetic: Lenti-D Drug Product Lenti-D Drug Product (autologous CD34+ cell-enriched population that conta |
| Recruiting |
: A Pilot Study of Vitamin D in Boys With X-linked Adrenoleukodystrophy : X-linked Adrenoleukodystrophy : 2015-10-29 : Dietary Supplement: vitamin D3 Daily oral supplement provided by study investigators |
| Completed |
: The Effect of Bezafibrate on the Level of Very Long Chain Fatty Acids (VLCFA) in X-linked Adrenoleukodystrophy (X-ALD) :
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| Withdrawn |
: Safety and Pharmacodynamic Study of Sobetirome in X-Linked Adrenoleukodystrophy (X-ALD) :
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| Terminated |
: A Phase III Trial of Lorenzo's Oil in Adrenomyeloneuropathy :
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