Hurler Syndrome - 22 Studies Found
Active, not recruiting |
: Intrathecal Enzyme Replacement for Hurler Syndrome : Hurler Syndrome : 2008-03-11 : Drug: IRT Laronidase Laronidase belongs to a class of drug |
Recruiting |
: Laronidase (Aldurazyme TM) Enzyme Replacement Therapy With Hematopoietic Stem Cell Transplant for Hurler Syndrome :
|
Completed |
: Stem Cell Transplant w/Laronidase for Hurler :
: 2005-09-12 :
|
Recruiting |
: Biomarker for Patients With Hurler Disease or High-grade Suspicion for Hurler Disease :
|
Active, not recruiting |
: Safety and Dose Ranging Study of Human Insulin Receptor MAb-IDUA Fusion Protein in Adults and Children With MPS I : Mucopolysaccharidosis I : 2017-02-09 : Drug: AGT-181 Human Insulin Receptor Monoclonal Antibody-Human alpha-L-iduronidase (HIRMAb-IDUA) Fusion |
Completed |
: Neurobehavioral Phenotypes in MPS III :
|
Completed |
: Clinical Study of Aldurazyme in Patients With Mucopolysaccharidosis (MPS) I :
|
Completed |
: Stem Cell Transplantation for Hurler :
|
Active, not recruiting |
: Safety and Dose Ranging Study of Insulin Receptor MAb-IDUA Fusion Protein in Patients With MPS I : Mucopolysaccharidosis I : 2015-02-19 : Drug: AGT-181 (HIRMAb-IDUA) intravenous infusion over 3-4 hours |