Beta-galactosidase-1 Deficiency - 6 Studies Found

Recruiting : Synergistic Enteral Regimen for Treatment of the Gangliosidoses
:
  • GM1 Gangliosidoses
  • GM2 Gangliosidoses
  • Drug: miglustat The Syner-G th
Recruiting : A Natural History Study of the Gangliosidoses
:
  • Tay-Sachs Disease
  • Sandhoff Disease
  • Late Onset Tay-Sachs Di
    : 2008-04-25
Recruiting : Biomarker for GM1/GM2 - Gangliosidoses
:
  • Gangliosidosis
  • GM1-Gangliosidosis
  • Gangliosidoses
  • Gaucher Disease

: 2002-01-27
Completed : Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders
:
  • Lysosomal Storage Disease
  • Peroxisomal Disorder

: 2012-06-20
:
  • Drug: Campath-1H A daily dose

Terminated : ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases
:
  • Inherited Metabolic Diseases
  • Lysosomal Storage Disorders
  • P
    : 2008-04-03
    : Biological: ALD-101 A subpopulation of cord blood cells composed of cells that express a high level of t