Deficiency Diseases - 33 Studies Found

Completed : Safety and Efficacy of Recombinant Human Acid Alpha-Glucosidase in the Treatment of Classical Infantile Pompe Disease
:
  • Pompe Disease
  • Glycogen Storage Disease Type II
  • Acid Maltas
    : 2001-10-31
    : Drug: recombinant human acid alpha-glucosidase (rhGAA)
Completed : rhGAA in Patients With Infantile-onset Glycogen Storage Disease-II (Pompe Disease)
:
  • Glycogen Storage Disease Type II
  • Pompe Disease
  • Acid Maltas
    : 2003-01-31
    : Biological: Myozyme 20 mg/kg to 40 mg/kg qow Other N
Recruiting : Clinical Biomarkers in Alpha-mannosidosis
: Alpha-Mannosidosis
: 2014-05-15
Completed : Long-term Efficacy and Safety of Lamazym for the Treatment of Patients With Alpha-Mannosidosis
: Alpha-Mannosidosis
: 2012-08-22
: Drug: Lamazym ERT, i.v. infusions weekly Other Names
Completed : A Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-Mannosidosis
: Alpha-Mannosidosis
: 2012-08-22
:
  • Drug: Lamazym ERT, i.v. infusi
Completed : Safety Study of Recombinant Human Alpha-mannosidase for the Treatment of Patients With Alpha-mannosidosis
: Alpha Mannosidosis
: 2010-12-29
: Drug: Lamazym Lamazym, ERT, infusion weekly Other Na
Recruiting : Trial on Safety and Efficacy of Velmanase Alfa Treatment in Pediatric Patients With Alpha-Mannosidosis
: Alpha-Mannosidosis
: 2016-11-25
: Drug: Velmanase Alfa (e.g. Lamazym) iv infusion treatment
Recruiting : Dose Finding Study of Recombinant Human Alpha-mannosidase for the Treatment of Patients With Alpha-mannosidosis
: Alpha Mannosidosis
: 2011-01-25
: Drug: Lamazym ERT, infusion weekly Other Name: rhLAM
Active, not recruiting : Lamazym Aftercare Study
: Alpha-Mannosidosis
: 2013-06-12
: Drug: Lamazym ERT, i.v. infusions weekly Other Names
Active, not recruiting : Lamazym Aftercare Study FR Designed to Provide Treatment for French Patients
: Alpha-Mannosidosis
: 2013-07-16
: Drug: Lamazym ERT, i.v. infusions weekly Other Names
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