Adrenoleukodystrophy - 26 Studies Found
| Completed |
: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation :
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| Completed |
: Stem Cell Transplant for Inborn Errors of Metabolism :
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| Completed |
: Betaine and Peroxisome Biogenesis Disorders : Peroxisome Biogenesis Disorders : 2013-03-29 : Drug: Betaine Betaine will be given orally (mixed with foo |
| RECRUITING |
: MT2022-01: MSCs for ALD : Cerebral Adrenoleukodystrophy : 2024-11-21 : Patients will receive 1 infusion (1 x 106 cells/kg on day 0) then be followed for 8 weeks from the infusion. |
| RECRUITING |
: Treating Leg Symptoms in Women With X-linked Adrenoleukodystrophy : Adrenoleukodystrophy : 2024-11-21 : Participants will be started on 0.125 mg pramipexole for the first week.If this dose is well tolerated but not effective, the dose can be increa |
| RECRUITING |
: A Clinical Study to Assess the Efficacy and Safety of Leriglitazone in Adult Male Subjects With Cerebral Adrenoleukodystrophy : Cerebral Adrenoleukodystrophy (cALD) : 2024-11-21 : Leriglitazone at a strength of 15 mg/ml.Once-daily dosing at an initial volume of 10 ml |