Mucopolysaccharidosis III - 25 Studies Found
Recruiting |
: Biomarker for Sanfilippo Disease :
|
Enrolling by invitation |
: An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093. :
: 2015-01-21 : Drug: HGT-1410 HGT-1410 administered according to Patient Group assignment. |
Recruiting |
: A Treatment Study of Mucopolysaccharidosis Type IIIB :
: 2016-02-27 : Drug: BMN 250 Chimeric fusion of recombinant human alpha-N-acetylglucosaminidase and truncated human ins |
Completed |
: Neurobehavioral Phenotypes in MPS III :
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Completed |
: Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using Multimodal Magnetic Resonance Imaging : MPS IIIB (Sanfilippo B Syndrome) : 2014-03-12 |
Recruiting |
: A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB) :
: Other: This is an observational study This is an observational study |