Mucopolysaccharidosis Type IIIB - 11 Studies Found
Recruiting |
: A Treatment Study of Mucopolysaccharidosis Type IIIB :
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Completed |
: Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B) : Sanfilippo Syndrome Type B : 2012-01-10 |
Recruiting |
: A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB) :
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Completed |
: A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB : MPS IIIB (Sanfilippo Syndrome) : 2014-11-03 |
Active, not recruiting |
: Natural History Study to Characterise the Course of Disease Progression in Patients With Mucopolysaccharidosis Type IIIB : MPS IIIB (Sanfilippo B Syndrome) : 2014-11-03 |
Active, not recruiting |
: Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in MPS IIIB : Mucopolysaccharidosis IIIB : 2014-12-15 : Drug: SBC-103 Other Name: recombinant human alpha-N-acetylglucosaminidase (rhNAGLU) |
Completed |
: Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using Multimodal Magnetic Resonance Imaging : MPS IIIB (Sanfilippo B Syndrome) : 2014-03-12 |
Active, not recruiting |
: A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 Administered Intravenously :
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Completed |
: Neurobehavioral Phenotypes in MPS III :
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