Adenosine Deaminase Deficiency - 18 Studies Found
| Completed |
: Gene Therapy ADA Deficiency : Adenosine Deaminase Deficiency : 2011-01-18 : Biological: Intravenous infusion of transduced cells Intravenous infusion of transduced cells |
| Completed |
: Treatment of SCID Due to ADA Deficiency With Autologous Transplantation of Cord Blood or Hematopoietic CD 34+ Cells After Addition of a Normal Human ADA cDNA by the EFS-ADA Lentiviral Vector :
|
| Withdrawn |
: Quality of Life and Neuropsychiatric Sequelae in Patients Treated With Gene Therapy for ADA-SCID and in Their Parents : ADA-SCID : 2010-08-14 |
| Recruiting |
: Autologous Cryopreserved CD34+ Hematopoietic Cells Transduced With EFS-ADA Lentivirus for ADA SCID : Severe Combined Immunodeficiency Due to ADA Deficiency : 2016-12-19 : Biological: Infusion of autologous cryopreserved EFS-ADA LV CD34+ cells Infusion of OTL-101 after reduce |
| Recruiting |
: EZN-2279 in Patients With ADA-SCID :
|
| Recruiting |
: Lentiviral Gene Therapy for Adenosine Deaminase (ADA) Deficiency :
|
| Active, not recruiting |
: Autologous Transplant of EFS-ADA Modified Bone Marrow Cells for ADA-Deficient Severe Combined Immunodeficiency (SCID) : ADA-SCID : 2013-05-07 : Genetic: EFS-ADA transduced CD34+ cells from the bone marrow Eligible subjects will undergo bone marrow |
| Completed |
: Gene Therapy for ADA-SCID : Severe Combined Immunodeficiency Syndrome : 2008-01-08 : Genetic: gene transduced PBL and/or gene transduced HSC infusions of autologous PBL and/or HSC transduce |
| Active, not recruiting |
: ADA Gene Transfer Into Hematopoietic Stem/Progenitor Cells for the Treatment of ADA-SCID : Immunologic Deficiency Syndromes : 2008-01-10 : Genetic: Gene transduced CD34+ cells infusion of autologous CD34+ cells transduced with retroviral vecto |
| Recruiting |
: Participation in a Research Registry for Immune Disorders :
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