Mucopolysaccharidoses - 25 Studies Found
Recruiting |
: Hematopoietic Stem Cell Transplantation for Mucopolysaccharidosis : Mucopolysaccharidosis : 2010-11-08 :
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Completed |
: Natural History Studies of Mucopolysaccharidosis III :
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Recruiting |
: A Study of JR-141 in Patients With Mucopolysaccharidosis Type II : Mucopolysaccharidosis II : 2017-04-10 : Drug: JR-141 IV infusion (lyophilized powder), 0.01-2.0 mg/kg/week |
Completed |
: Study of rhASB in Patients With Mucopolysaccharidosis VI : Mucopolysaccharidosis VI : 2005-02-24 :
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Recruiting |
: Mucopolysaccharidosis I (MPS I) Registry : Mucopolysaccharidosis I (MPS I) : 2005-09-02 |
Not yet recruiting |
: Mucopolysaccharidosis (MPS) Screening in a High-Risk Population With Previous Surgical Repair or Presence of Inguinal and/or Umbilical Hernia Combined With Pediatric ENT Surgery or Bronchoscopy : Mucopolysaccharidoses : 2017-01-09 |
Terminated |
: Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA : Mucopolysaccharidosis Type IVA : 2012-11-21 |
Completed |
: Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease :
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Completed |
: Immune Tolerance Study With Aldurazyme® (Laronidase) : Mucopolysaccharidosis I : 2008-08-13 :
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Completed |
: An Open-Label Phase 1/2 Study to Assess the Safety, Efficacy and Dose of Study Drug UX003 Recombinant Human Beta-glucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With MPS 7 : Mucopolysaccharidosis Type 7 : 2013-05-08 : Drug: UX003 |