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Gaucher Disease Type 3 - 8 Studies Found
Estado | Estudiar |
Recruiting |
Nombre del estudio: GZ/SAR402671 in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 Condición: Gaucher Disease Type 1-Gaucher Disease Type 3 Fecha: 2016-07-20 Intervenciones: Drug: GZ402671 Other Name: Venglustat |
Recruiting |
Nombre del estudio: The Effect of Velaglucerase Alfa (Vpriv) on Skeletal Development in Pediatric Gaucher Disease Condición:
Fecha: 2015-07-28 Intervenciones: Drug: Velaglucerase alfa Enzyme replacement therapy |
Completed |
Nombre del estudio: OGT 918-006: A Phase I/II Randomized, Controlled Study of OGT 918 in Patients With Neuronopathic Gaucher Disease Condición: Gaucher Disease Fecha: 2002-07-09 Intervenciones: Drug: OGT 918 |
Completed |
Nombre del estudio: Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease Condición: Gaucher Disease, Type 3 Fecha: 2012-09-10 Intervenciones: Biological: velaglucerase alfa lyophilized powder, intravenous infusion, units, Every other week (EOW) |
Completed |
Nombre del estudio: Effects of Enzyme Replacement in Gaucher's Disease Condición: Gaucher's Disease Fecha: 1999-11-03 |
Completed |
Nombre del estudio: PEG-Glucocerebrosidase for the Treatment of Gaucher Disease Condición: Gaucher's Disease Fecha: 1999-11-03 Intervenciones: Drug: Lysodase |
Completed |
Nombre del estudio: Convection-Enhanced Delivery of Glucocerebrosidase to Treat Type 2 Gaucher Disease Condición: Type 2 Gaucher Disease Fecha: 2005-10-26 |
Completed |
Nombre del estudio: Study to Evaluate Blood Cell Lines From Patients With Gaucher Disease Condición: Gaucher Disease Fecha: 2006-07-10 Intervenciones: Procedure: Blood sample |